Menu
ABOUT US
Who We Are
Gene Editing
Leadership
Corporate Responsibility
Partnerships
News
Contact
Therapies
Pipeline
FOCUS AREAS
Hemoglobinopathies
Immuno-Oncology
Autoimmune
In Vivo
Regenerative Medicine
CRISPR-X
PATIENTS
Patient Advocacy
Community Voices
Current Clinical Research
Expanded Access to Investigational Medicines
Careers
Investors
Demo Page
TIME BEST INVENTIONS
2024
FIERCE50 HONOREE IN INNOVATION
2024
NEVY AWARD IN PATIENT IMPACT
2024
SCRIP AWARD
2024
Previous Slide
Next Slide