Over a Decade of Innovation
We are pioneering a new era of medicines
Transforming the lives of patients living with serious diseases
Across a number of disease areas
1
Approved
Therapy
5
Clinical
Programs
10
Preclinical
Programs
Rapidly translating a revolutionary technology into therapies
Innovation that matters
Rapidly translating a revolutionary technology into therapies
Learn more about gene editing
Pushing the bounds of science
We are pioneers of the CRISPR technology and at the forefront of what’s next
Learn more about CRISPR-XLearn more about our programs
We have established a diverse portfolio across a broad range of disease areas including hemoglobinopathies, oncology, diabetes and cardiovascular disease.
View PipelineRECOGNIZED FOR EXCELLENCE
We take pride in delivering outstanding work, and it's an honor to have our efforts recognized. Our awards celebrate innovation, dedication, and excellence in our industry. Here are some of the accolades we've earned along the way.

TIME BEST INVENTIONS 2024

FIERCE50 HONOREE IN INNOVATION 2024

NEVY AWARD IN PATIENT IMPACT 2024
